Activity Details

Free CME
0.5 AMA PRA Category 1 Credit(s)
Released: August 29, 2019
Expires: August 28, 2020
30 minutes to complete

Accredited By

Target Audience

This activity is intended for neurologists, neuromuscular specialists, and pediatric neurologists.

Learning Objectives

After completing this activity, the participant should be better able to:

  • Explain how gene therapy works
  • Explain the potential implications of gene therapy for SMA
  • Summarize key clinical trial data on emerging treatments for SMA, with a focus on gene therapy

Activity Description

This multi-media activity will explore the latest in SMA treatment, including the newly approved gene therapy. Hear from 3 experts in the field as they explain what you need to know about this treatment. Hear answers to the most frequently asked questions on this topic and access tools and resources you will be able to use in your practice today.

Statement of Educational Need

Spinal muscular atrophy (SMA) is the most common fatal genetic disease of children under 2 years old, though gene therapy has led to babies hitting unprecedented motor milestones and living longer. The first gene therapy is now available to treat SMA and it is critical that clinicians are prepared to administer this treatment.


Gyula Acsadi, MD, PhD-Content Creator and Presenter
Professor of Pediatrics and Neurology
University of Connecticut School of Medicine
Division Head, Neurology
Connecticut Children’s Medical Center
Farmington, CT

Wendy K. Chung, MD, PhD-Content Creator and Presenter
Kennedy Family Professor of Pediatrics and Medicine
Columbia University
New York, NY

Julie Parsons, MD-Content Creator and Presenter
Co-Director, Neuromuscular Clinic
Haberfeld Family Endowed Chair in Pediatric Neuromuscular Disorders
Children’s Hospital Colorado
Professor of Clinical Pediatrics and Neurology
University of Colorado
Aurora, CO

Conflict of Interest Policy/Disclosure Statement

In accordance with the ACCME Standards for Commercial Support, The France Foundation (TFF) requires that individuals in a position to control the content of an educational activity disclose all relevant financial relationships with any commercial interest. TFF resolves all conflicts of interest to ensure independence, objectivity, balance, and scientific rigor in all its educational programs. Furthermore, TFF seeks to verify that all scientific research referred to, reported, or used in a CME/CE activity conforms to the generally accepted standards of experimental design, data collection, and analysis. TFF is committed to providing learners with high-quality CME/CE activities that promote improvements in healthcare and not those of a commercial interest.

Activity Staff Disclosures
The planners, reviewers, editors, staff, CME committee, or other members at The France Foundation who control content have no relevant financial relationships to disclose.

Faculty Disclosures-Content Creators
The faculty listed below report that they have no relevant financial relationships to disclose:

  • Wendy K. Chung, MD, PhD

The following faculty report that they have relevant financial relationships to disclose:

  • Gyula Acsadi, MD, PhD, reports that he has done consulting for Biogen, Serepta, and AveXis; served on a Speakers Bureau for Biogen; and has done contract research for Biogen, Serepta, and Italfarmaco.
  • Julie Parsons, MD, reports that she has served on advisory boards for AveXis, Biogen, and Genentech. She has done contract research for AveXis, Biogen, Scholar Rock, and Cytokinetics.

Accreditation Statement

The France Foundation is accredited by the Accreditation Council for Continuing Medical Education (ACCME) to provide continuing medical education for physicians.

Designation of Credit

The France Foundation designates this enduring activity for a maximum of 0.5 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Nurses who are certified by the American Nurses Credentialing Center (ANCC) may utilize activities that are certified by ACCME-accredited providers toward their requirement for certification renewal by the ANCC. A certificate of attendance will be provided by The France Foundation, an ACCME-accredited provider.

Instructions for Receiving Credit

  • There are no fees for participating in and receiving credit for this activity.
  • Review the activity objectives and CME/CE information.
  • Complete the CME/CE activity.
  • Complete the online posttest. A score of at least 75% is required to successfully complete this activity. The participant may take the test until successfully passed.
  • Complete the CME/CE evaluation/attestation form, which provides each participant with the opportunity to comment on how participating in the activity will affect their professional practice; the quality of the instructional process; the perception of enhanced professional effectiveness; the perception of commercial bias; and his/her views on future educational needs.
  • Credit documentation/reporting:
    • If you are requesting AMA PRA Category 1 Credits™ or a certificate of participation—your CME/CE certificate will be available for download.

Statement of Commercial Support

This activity is supported by an educational grant from AveXis.

Disclaimer Statement/ Disclosure of Unlabeled Use

TFF requires CME faculty (speakers) to disclose when products or procedures being discussed are off label, unlabeled, experimental, and/or investigational, and any limitations on the information that is presented, such as data that are preliminary, or that represent ongoing research, interim analyses, and/or unsupported opinion. Faculty in this activity may discuss information about pharmaceutical agents that is outside of U.S. Food and Drug Administration approved labeling. This information is intended solely for continuing medical education and is not intended to promote off-label use of these medications. TFF does not recommend the use of any agent outside of the labeled indications. If you have questions, contact the Medical Affairs Department of the manufacturer for the most recent prescribing information.

Contact Information for Questions about the Activity

For questions about the activity, please contact The France Foundation at 800-230-0721 or

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